The road from laboratory discoveries to drugs to treat patients might more accurately be described as a treacherous mountain path. Many experiments that appear promising in a Petri dish don’t work in mice. And compounds that are safe and effective in rodents won’t necessarily prove out in people. The U.S. drug industry’s trade organization, the […]
rare diseases
OMRF, OUHSC scientists find gene at the root of rare disease
Exome sequencing helps pinpoint previously unknown genetic links
